Program: 953,177 results found.
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BioMarin Morquio A Program
BioMarin is currently investigating a potential treatment to benefit patients diagnosed with mucopolysaccharidosis IVA (MPS IVA), also known as Morquio A syndrome. BioMarin’s initial development plans include two studies: MorCAP (a clinical assessment program) and a Phase 1/2 clinical trial.
Morquioasyndrome.com ~
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morquiobmrn.com
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